Thank you for your interest in the externally-led Patient-Focused Drug Development (PFDD) Meeting on Barth syndrome!
Barth syndrome (BTHS) affected individuals and their families have a unique opportunity to have their voices heard by the US Food and Drug Administration (FDA) on Wednesday, July 18th, in Clearwater Beach, Florida, from 12:00 - 5:00 PM EDT. The PFDD meeting is designed to educate the Barth Syndrome Foundation researchers and FDA, whose representatives will be present both in-person and via the live webcast, to accelerate the development and approval of life-changing therapies for people affected by BTHS.
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