Clinical Research and Their Impact on Treatment

Clinical trials — An overview
Kate McCurdy, BSF Scientific & Medical Advisory Board, Emerita

Characterization of the metabolic phenotype in individuals with Barth syndrome with and without cardiac transplantation
W. Todd Cade, PT, PhD, Washington University School of Medicine, St. Louis, MO

Functional exercise capacity, strength, balance and motion reaction time in Barth syndrome: Outcomes from the 2016 Barth Syndrome Foundation Scientific, Medical & Family Conference
Brittany DeCroes Hornby, PT, DPT, PCS, Kennedy Krieger Institute, Baltimore, MD

Impact on the family and quality of life: Findings from the 2014 and 2016 surveys
Yoonjeong Lim, PhD, OTR/L, Georgia State University, Atlanta, GA

Discussions/Questions & Answers